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Exagamglogene Autotemcel for Severe Sickle Cell Disease
The New England Journal of Medicine ( IF 158.5 ) Pub Date : 2024-04-24 , DOI: 10.1056/nejmoa2309676 Haydar Frangoul 1 , Franco Locatelli 1 , Akshay Sharma 1 , Monica Bhatia 1 , Markus Mapara 1 , Lyndsay Molinari 1 , Donna Wall 1 , Robert I. Liem 1 , Paul Telfer 1 , Ami J. Shah 1 , Marina Cavazzana 1 , Selim Corbacioglu 1 , Damiano Rondelli 1 , Roland Meisel 1 , Laurence Dedeken 1 , Stephan Lobitz 1 , Mariane de Montalembert 1 , Martin H. Steinberg 1 , Mark C. Walters 1 , Michael J. Eckrich 1 , Suzan Imren 1 , Laura Bower 1 , Christopher Simard 1 , Weiyu Zhou 1 , Fengjuan Xuan 1 , Phuong Khanh Morrow 1 , William E. Hobbs 1 , Stephan A. Grupp 1
The New England Journal of Medicine ( IF 158.5 ) Pub Date : 2024-04-24 , DOI: 10.1056/nejmoa2309676 Haydar Frangoul 1 , Franco Locatelli 1 , Akshay Sharma 1 , Monica Bhatia 1 , Markus Mapara 1 , Lyndsay Molinari 1 , Donna Wall 1 , Robert I. Liem 1 , Paul Telfer 1 , Ami J. Shah 1 , Marina Cavazzana 1 , Selim Corbacioglu 1 , Damiano Rondelli 1 , Roland Meisel 1 , Laurence Dedeken 1 , Stephan Lobitz 1 , Mariane de Montalembert 1 , Martin H. Steinberg 1 , Mark C. Walters 1 , Michael J. Eckrich 1 , Suzan Imren 1 , Laura Bower 1 , Christopher Simard 1 , Weiyu Zhou 1 , Fengjuan Xuan 1 , Phuong Khanh Morrow 1 , William E. Hobbs 1 , Stephan A. Grupp 1
Affiliation
Exagamglogene autotemcel (exa-cel) is a nonviral cell therapy designed to reactivate fetal hemoglobin synthesis by means of ex vivo clustered regularly interspaced short palindromic repeats (CRISPR...
中文翻译：
Exagamglogene Autotemcel 治疗严重镰状细胞病
Exagamglogene autotemcel (exa-cel) 是一种非病毒细胞疗法，旨在通过离体成簇规则间隔短回文重复序列 (CRISPR...
更新日期：2024-04-25
中文翻译：
Exagamglogene Autotemcel 治疗严重镰状细胞病
Exagamglogene autotemcel (exa-cel) 是一种非病毒细胞疗法，旨在通过离体成簇规则间隔短回文重复序列 (CRISPR...
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